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Vamorolone trial in Duchenne muscular dystrophy shows dose-related improvement in muscle function
Hoffman EP1, Schwartz BD2, Mengle-Gaw LJ2, Smith EC2, Castro D2, Mah JK2, McDonald CM2, Kuntz NL2, Finkel RS2, Guglieri M2, Bushby K2, Tulinius M2, Nevo Y2, Ryan MM2, Webster R2, Smith AL2, Morgenroth LP2, Arrieta A2, Shimony M2, Siener C2, Jaros M2, Shale P2, McCall JM2, Nagaraju K2, van den Anker J2, Conklin LS2, Cnaan A2, Gordish-Dressman H2, Damsker JM2, Clemens PR2; Cooperative International Neuromuscular Research Group.